EspeRare is a not-for-profit organization established in Switzerland and recognized to be operating in the public interest. In collaboration with patient groups and other key stakeholders, EspeRare focuses on rescuing and repositioning discontinued therapies with high potential to address severe and currently neglected therapeutic needs of children affected by rare genetic diseases. EspeRare is using its pharma R&D expertise and patient-centric model to advance novel treatments for the undeserved patients, thus bringing hope for better future to these children and their families.